| Item Type | Name |
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Concept
|
Acetylcysteine
|
|
Concept
|
Adenosine Triphosphate
|
|
Concept
|
Antioxidants
|
|
Concept
|
Base Sequence
|
|
Concept
|
Clone Cells
|
|
Concept
|
Diaphragm
|
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Concept
|
Cardiomegaly
|
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Concept
|
Exons
|
|
Concept
|
Drosophila melanogaster
|
|
Concept
|
Fibroblasts
|
|
Concept
|
Glioblastoma
|
|
Concept
|
Obesity
|
|
Concept
|
Hydrogen Peroxide
|
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Concept
|
Energy Metabolism
|
|
Concept
|
Hexokinase
|
|
Concept
|
Isoenzymes
|
|
Concept
|
Myotonic Dystrophy
|
|
Concept
|
Mice, Transgenic
|
|
Concept
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Mice, Inbred C57BL
|
|
Concept
|
Mutation
|
|
Concept
|
Myocardial Contraction
|
|
Concept
|
Mitochondria, Heart
|
|
Concept
|
Muscle Proteins
|
|
Concept
|
Pressure
|
|
Concept
|
RNA Splicing
|
|
Concept
|
Humans
|
|
Concept
|
Genetic Variation
|
|
Concept
|
Protein Engineering
|
|
Concept
|
Transduction, Genetic
|
|
Concept
|
Cell Culture Techniques
|
|
Concept
|
Reverse Transcriptase Polymerase Chain Reaction
|
|
Concept
|
Oligodeoxyribonucleotides, Antisense
|
|
Concept
|
Guanine Nucleotide Exchange Factors
|
|
Concept
|
Muscle Development
|
|
Concept
|
Mitochondria
|
|
Concept
|
Gene Expression
|
|
Concept
|
Rats, Sprague-Dawley
|
|
Concept
|
RNA Interference
|
|
Concept
|
Alternative Splicing
|
|
Concept
|
Treatment Outcome
|
|
Concept
|
Muscular Dystrophies
|
|
Concept
|
Reading Frames
|
|
Concept
|
Point Mutation
|
|
Concept
|
Sequence Deletion
|
|
Concept
|
MyoD Protein
|
|
Concept
|
Synaptosomal-Associated Protein 25
|
|
Concept
|
Death Domain Receptor Signaling Adaptor Proteins
|
|
Concept
|
Muscular Dystrophy, Duchenne
|
|
Concept
|
Reactive Oxygen Species
|
|
Concept
|
Primary Cell Culture
|
|
Concept
|
Green Fluorescent Proteins
|
|
Concept
|
Targeted Gene Repair
|
|
Concept
|
Microscopy, Confocal
|
|
Concept
|
Indoleamine-Pyrrole 2,3,-Dioxygenase
|
|
Concept
|
Catalytic Domain
|
|
Concept
|
Progeria
|
|
Concept
|
Mice
|
|
Concept
|
Sarcolemma
|
|
Concept
|
HEK293 Cells
|
|
Concept
|
Rats
|
|
Concept
|
ARNTL Transcription Factors
|
|
Concept
|
Muscular Dystrophies, Limb-Girdle
|
|
Concept
|
Insulin-Secreting Cells
|
|
Concept
|
Blotting, Western
|
|
Concept
|
Hypoxia-Inducible Factor 1
|
|
Concept
|
Dystrophin
|
|
Concept
|
Transfection
|
|
Concept
|
Genetic Therapy
|
|
Concept
|
Myocardial Reperfusion Injury
|
|
Concept
|
Cell Hypoxia
|
|
Concept
|
Gene Expression Regulation, Enzymologic
|
|
Concept
|
Codon, Nonsense
|
|
Concept
|
Sarcoglycanopathies
|
|
Concept
|
Morpholinos
|
|
Concept
|
CLOCK Proteins
|
|
Concept
|
Cell Line, Tumor
|
|
Concept
|
Brain Neoplasms
|
|
Concept
|
Calcium
|
|
Concept
|
Cell Line
|
|
Concept
|
Cell Survival
|
|
Concept
|
Cells, Cultured
|
|
Concept
|
Disease Models, Animal
|
|
Concept
|
Glucose
|
|
Concept
|
Heterozygote
|
|
Concept
|
Microscopy, Fluorescence
|
|
Concept
|
Recombinant Fusion Proteins
|
|
Concept
|
Urine
|
|
Concept
|
Genetic Predisposition to Disease
|
|
Concept
|
Sarcoglycans
|
|
Concept
|
Membrane Potential, Mitochondrial
|
|
Academic Article
|
Reengineering a transmembrane protein to treat muscular dystrophy using exon skipping.
|
|
Academic Article
|
Welcome to the splice age: antisense oligonucleotide-mediated exon skipping gains wider applicability.
|
|
Academic Article
|
Direct reprogramming of urine-derived cells with inducible MyoD for modeling human muscle disease.
|
|
Academic Article
|
Meeting Report: New Directions in Biology and Disease of Skeletal Muscle 2014.
|
|
Academic Article
|
Meeting Report: New Directions in the Biology and Disease of Skeletal Muscle 2014.
|
|
Academic Article
|
Efficient exon skipping of SGCG mutations mediated by phosphorodiamidate morpholino oligomers.
|
|
Academic Article
|
Reduction in hexokinase II levels results in decreased cardiac function and altered remodeling after ischemia/reperfusion injury.
|
|
Academic Article
|
Regulation and cytoprotective role of hexokinase III.
|
|
Academic Article
|
Hexokinase II knockdown results in exaggerated cardiac hypertrophy via increased ROS production.
|
|
Academic Article
|
Mutation-Based Therapy for Duchenne Muscular Dystrophy: Antisense Treatment Arrives in the Clinic.
|
|
Academic Article
|
Distinct pathological signatures in human cellular models of myotonic dystrophy subtypes.
|
|
Academic Article
|
A gene-edited mouse model of limb-girdle muscular dystrophy 2C for testing exon skipping.
|
|
Academic Article
|
A role for alternative splicing in circadian control of exocytosis and glucose homeostasis.
|
|
Academic Article
|
Immunosuppressive IDO in Cancer: Mechanisms of Action, Animal Models, and Targeting Strategies.
|
|
Academic Article
|
Erratum: A role for alternative splicing in circadian control of exocytosis and glucose homeostasis.
|
|
Concept
|
Gene Editing
|
|
Concept
|
Clustered Regularly Interspaced Short Palindromic Repeats
|